Correction of the Exon 2 Duplication in DMD Myoblasts by a Single CRISPR/Cas9 System

Nom de la revue
Molecular Therapy - Nucleic Acids
Annalisa Lattanzi, Stephanie Duguez, Arianna Moiani, Araksya Izmiryan, Elena Barbon, Samia Martin, Kamel Mamchaoui, Vincent Mouly, Francesco Bernardi, Fulvio Mavilio, Matteo Bovolenta